By Nick Paul Taylor
Decibel Therapeutics has netted $127 million from public investors to develop gene therapies that use a surgical delivery method. The IPO haul will enable Decibel to take a gene therapy treatment for a genetic form of profound hearing loss into clinical trials.
read more
By Nick Paul Taylor
Advanced Chemotherapy Technologies (ACT) has raised money to fund clinical development of its method for delivering gemcitabine directly to tumors. ACT sees the technology as a way to deliver a fatal dose of chemotherapy to tumor cells without causing the side effects associated with systemic administration.
read more
By Nick Paul Taylor
Tonix Pharmaceuticals has licensed oxytocin-based therapeutic technology for the treatment of rare genetic disorder Prader-Willi syndrome. The agreement with French research institute Inserm continues Tonix’s push to expand the use of its nasal oxytocin delivery capabilities.
read more
By Ben Adams
Neurodegenerative biotech and pharma friend Denali has revealed a positive peek at some early Hunter syndrome data.
read more
Sponsored By: Within3
We enable virtual work — offering over-time sessions where participants are more focused, insights are more diverse and business goals are met.
Sponsored by: Catalent
Discover the current state of patient-focused dose design through clinical evidence, real-world case studies and patient preference-driven drug design solutions that can help develop better treatments and successful real-world outcomes.
Sponsored by: Catalent
This eBook features insights from experts in the industry on patient-centric drug development challenges and strategies on advancing drug design and development effectively.
Sponsored By: Medidata, a Dassault Systèmes company
8 parameters to optimize your “Path to Virtualization” across site- and patient-centric capabilities in this Sponsor Edition eBook.
Sponsored By: LabVantage Solutions
Uncover the real impact of “digital transformation” with practical advice to help you plan your own transformative journey to a harmonized digital ecosystem.
Sponsored By: Acorn AI, a Medidata Company
Acorn AI has developed a flexible and scalable Commercial Data Model that provides pharmaceutical companies with the data-driven insights required to respond to the industry’s ever-changing landscape. Download the whitepaper to learn how Acorn AI’s intuitive data model enables launch success and more.
Sponsored by: Catalent
Learn about drug product process development challenges and risks, the difference between innovator and biosimilar drug product process development, and more during the drug product process development phase.
Sponsored by: Catalent
In this webinar, pharmaceutical scientists present real-life examples of challenges they’ve overcome in the transfer of oral small molecules from a dedicated early-phase development site to a dedicated late-phase manufacturing site.
