Today's Rundown Vertex, CRISPR’s gene-editing treatment for blood disorders shows promise in early data Bischofberger-helmed Kronos nabs Celgene research exec as new CMO Werewolf Therapeutics uncloaks with $56M and shape-shifting cancer meds GHO raises €975M European healthcare fund Tissium raises €39M to advance tech with drug delivery uses Sanofi to assimilate Aetion's real-world data platform into its own Lilly putting $400M into U.S. diabetes production, adding 100 jobs Featured Story | | | Wednesday, November 20, 2019 CRISPR Therapeutics and Vertex Pharmaceuticals unveiled early data from the first company-backed study to test a CRISPR-based medicine in humans. The data, from two patients with severe blood disorders, are "promising” for what could be a one-and-done treatment for patients who need chronic care, wrote Cantor Fitzgerald analysts in a note. |
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Top Stories Wednesday, November 20, 2019 Fierce 15 winner Kronos Bio has poached Jorge DiMartino, M.D., Ph.D., as its chief medical officer and executive vice president of clinical development. Wednesday, November 20, 2019 It’s a full moon for Werewolf Therapeutics as the company comes out of stealth with $56 million and an approach it believes can cut through the toxic effects that have limited the use of certain cancer-killing agents. It is working on medicines that are delivered systemically but stay inactive within the body until they reach a tumor. Wednesday, November 20, 2019 GHO Capital has raised €975 million ($1.1 billion) to invest in European healthcare companies. The fund will back pharma companies as well as developers of medtech products and providers of outsourced services. Wednesday, November 20, 2019 Tissium has raised €38.8 million ($42.9 million) to fund work on synthetic programmable polymers with applications in drug delivery and other areas. The money will fund work to develop polymers in multiple indications and an associated U.S. expansion. Wednesday, November 20, 2019 Sanofi is launching a companywide project to incorporate its real-world data platform with Aetion’s analytics system to better develop studies capable of standing up to regulatory requirements. Wednesday, November 20, 2019 Eli Lilly faced critics of rising insulin prices this year by introducing a generic version of its popular Humalog priced at half the cost. Now the drugmaker is investing $400 million in its Indianapolis production site so it can make more diabetes treatments and prepare for pipeline products. 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